LAL Deficiency (Lysosomal Acid Lipase Disease) & Wolman Disease patient support
I'm a new member here and not sure I'm writing on the right page but still I hope I can get a feed-back.
I'm from Ukraine. My son (almost 6 years old) was diagnosed CESD. 1.5 years ago we were the first in our country, at the moment there are 6 patients in total.
Can everyone tell me in what countries Kanuma is used already for treatment? What are the results? Do all the patients receive treating?
Added by Tatyana on October 20, 2017 at 2:04am — No Comments